Clinical DevelopmentArrowhead's next-gen TRiM platform enables subcutaneous dosing, showing high concentrations of siRNA in the deep brain region, which is a significant advancement over traditional methods.
Pipeline ExpansionArrowhead is expanding its cardiometabolic franchise with plans to advance two obesity candidates to Phase 1/2 programs, supported by preclinical data demonstrating the potential of its TRiM platform.
Trial ResultsPlozasiran treatment led to a statistically significant reduction in the incidence of acute pancreatitis compared to placebo, highlighting its potential as a best-in-class treatment for familial chylomicronemia syndrome.