FDA ApprovalIonis announced FDA approval of olezarsen (Tryngolza) for the treatment of familial chylomicronemia syndrome (FCS), marking it as the first FDA approved therapy for this rare disease in the US.
Financial PositionThe company has a net debt to total capital ratio of 0%, indicating a strong financial position.
Market PotentialThe FCS approval provides Ionis with a hedge against future data, suggesting potential for significant US sales if ultra-orphan pricing is maintained.