Financial Performance3Q24 revenue exceeded expectations meaningfully, in part due to steady sales of Emflaza despite it now having generic competition.
Pipeline DevelopmentsPTC continues to execute well, with Upstaza's PDUFA and sepiapterin's set for future approval, and anticipate approval for both.
Product ApprovalKebilidi was approved with a broad label, enabling the treatment of children and adults across the spectrum of disease severity.