Drug Approval And Market PotentialThe FDA has fast tracked potential approval for vatiquinone, the company’s drug to treat Friedrich ataxia, providing some de-risking for the FA program.
Sales PerformanceQ3 revenue was $197MM beating consensus of $172MM driven by strong protection of Emflaza sales.
Strategic PartnershipsPTC signed an exclusive global license agreement with NVS for PTC518 in Huntington's disease in exchange for $1B upfront, up to $1.9B in development, regulatory and sales milestones, a 40/60 profit share in the U.S., and double-digit tiered royalties ex-U.S.