Strong Financial Performance
Fourth quarter revenue totaled $213 million, and full year 2024 revenue was $807 million, exceeding guidance. The company ended 2024 with over $1.1 billion in cash and received an additional $1 billion in January from the Novartis transaction.
Successful Regulatory Milestones
PTC submitted four approval applications to the FDA, all accepted for review, including KEBILIDI, Sepiapterin, Translarna, and Vatiquinone. KEBILIDI was approved in November.
Strategic Partnership with Novartis
PTC announced a collaboration with Novartis for the PTC518 Huntington's disease program, receiving $1 billion upfront and is eligible for up to $1.9 billion in development and sales milestones.
Exciting Prospects for 2025
PTC anticipates global launch of Sepiapterin, potential launch of Vatiquinone, and 12-month results from PIVOT-HD study.