Competitive AdvantageDYNE-251 offers a competitive advantage with a once-a-month dose compared to high-frequency dosing of current standards of care.
Efficacy And SafetyDYNE-251 demonstrates sustained clinical improvement and stabilization in key clinical endpoints, showing potentially best-in-class efficacy with a significant increase in dystrophin expression.
Regulatory ProgressThe registrational cohort for DYNE-251 is fully enrolled, with expectations to submit the BLA for potential accelerated approval in the US.