Drug Development And ApprovalPlozasiran's best-in-class characteristics on efficacy, quarterly dosing, and side effect profile make it well-positioned to become the standard-of-care in FCS if approved.
Financial Stability And PartnershipsThe partnership with SRPT provides a significant cash infusion of over $1.1 billion, strengthening the company's balance sheet for future milestones.
Research And Development ProgressThe company's R&D engine continues to show productivity, generating compelling next or best-in-class programs.