Collaborative DevelopmentSolid announced a collaboration with Mayo Clinic to develop an AAV gene therapy platform for therapies to treat sudden cardiac death-predisposing genetic cardiomyopathies and channelopathies.
Innovative Treatment StrategyThe dual administration strategy of SGT-212, involving both intravenous infusion and MRI-guided injection, could effectively treat both neurological and cardiac symptoms of FA.
Regulatory SupportThe FDA has approved Solid Biosciences' IND application for SGT-212, a gene therapy for Friedreich's ataxia, showing regulatory support for the treatment.