Drug Development And InnovationRGX-202 is differentiated in its design versus other DMD gene therapies by its CT domain microdystrophin construct, presenting an interesting potential opportunity.
Financial Position And Market PotentialRGNX ended with $278.6mm in cash and equivalents, expected to fund operations, indicating a strong financial position.
Regulatory And Financial MilestonesAn EOP2 meeting with the FDA regarding ABBV-RGX-314 in DR is upcoming and should open the door for a pivotal trial initiation, triggering a hefty $200M milestone payment from AbbVie.