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Ultragenyx Pharmaceutical (RARE)
NASDAQ:RARE

Ultragenyx Pharmaceutical (RARE) Price & Analysis

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RARE Stock Chart & Stats


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Bulls Say, Bears Say

Bulls Say
Financial PerformanceUltragenyx provided a strong revenue growth guidance with expected 17% year-over-year growth at the midpoint for FY25.
Product LaunchUX111 could be Ultragenyx's first gene therapy launch, setting the stage for several other programs in the pipeline.
Regulatory MilestoneThe FDA has accepted the BLA of UX111 for Priority Review under an accelerated approval pathway, indicating a significant regulatory milestone for Ultragenyx.
Bears Say
Clinical Trial UncertaintyThere is a focus on the second interim analysis for setrusumab in mid-2025, while the pipeline continues to progress nicely.
Commercial VariabilityThere is a reiterated Buy rating with a price objective of $83, indicating confidence in the stock's future performance.
Investment RisksThere are risks to the investment thesis, including potential clinical trial failures, failure to secure regulatory approvals, and smaller than anticipated commercial opportunities.
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Financials

Quarterly

Ownership Overview

4.14%29.07%35.83%17.21%
35.83% Other Institutional Investors
17.21% Public Companies and
Individual Investors

Risk Analysis

Main Risk Category
Tech & InnovationRisks related to the company’s reliance on technology and ability to make innovative products

Website Traffic

Sorry, No Data Available
There is no website visitor data available for this stock.
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RARE FAQ

What was Ultragenyx Pharmaceutical’s price range in the past 12 months?
Ultragenyx Pharmaceutical lowest stock price was $30.46 and its highest was $60.37 in the past 12 months.
    What is Ultragenyx Pharmaceutical’s market cap?
    Ultragenyx Pharmaceutical’s market cap is $3.05B.
      When is Ultragenyx Pharmaceutical’s upcoming earnings report date?
      Ultragenyx Pharmaceutical’s upcoming earnings report date is May 01, 2025 which is in 22 days.
        How were Ultragenyx Pharmaceutical’s earnings last quarter?
        Ultragenyx Pharmaceutical released its earnings results on Feb 13, 2025. The company reported -$1.39 earnings per share for the quarter, missing the consensus estimate of -$1.308 by -$0.082.
          Is Ultragenyx Pharmaceutical overvalued?
          According to Wall Street analysts Ultragenyx Pharmaceutical’s price is currently Undervalued. Get more investment ideas with TipRanks Premium
            Does Ultragenyx Pharmaceutical pay dividends?
            Ultragenyx Pharmaceutical does not currently pay dividends.
            What is Ultragenyx Pharmaceutical’s EPS estimate?
            Ultragenyx Pharmaceutical’s EPS estimate is -1.57.
              How many shares outstanding does Ultragenyx Pharmaceutical have?
              Ultragenyx Pharmaceutical has 93,899,666 shares outstanding.
                What happened to Ultragenyx Pharmaceutical’s price movement after its last earnings report?
                Ultragenyx Pharmaceutical reported an EPS of -$1.39 in its last earnings report, missing expectations of -$1.308. Following the earnings report the stock price went down -2.367%.
                  Which hedge fund is a major shareholder of Ultragenyx Pharmaceutical?
                  Currently, no hedge funds are holding shares in RARE
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                  Company Description

                  Ultragenyx Pharmaceutical

                  Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Europe, and internationally. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and adults with Mucopolysaccharidosis VII; Dojolvi for treating long-chain fatty acid oxidation disorders; and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia. The company's products candidatures include DTX401, an adeno-associated virus 8 (AAV8) gene therapy clinical candidate for the treatment of patients with glycogen storage disease type Ia; DTX301, an AAV8 gene therapy for the treatment of patients with ornithine transcarbamylase; UX143, a human monoclonal antibody for the treatment of osteogenesis imperfecta; GTX-102, an antisense oligonucleotide for the treatment of Angelman syndrome; UX701, for the treatment of Wilson disease; and UX053 for the treatment of glycogen storage disease type III. Ultragenyx Pharmaceutical Inc. has collaboration and license agreement with Kyowa Kirin Co., Ltd.; Saint Louis University; Baylor Research Institute; REGENXBIO Inc.; Bayer Healthcare LLC; GeneTx; Mereo; University of Pennsylvania; Arcturus Therapeutics Holdings Inc., Solid Biosciences Inc.; and Daiichi Sankyo Co., Ltd. Ultragenyx Pharmaceutical Inc. was incorporated in 2010 and is headquartered in Novato, California.
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                  RARE Company Deck

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                  RARE Earnings Call

                  Q4 2025
                  0:00 / 0:00
                  Earnings Call Sentiment|Positive
                  The earnings call reflected strong revenue growth and successful international expansion, alongside notable advancements in clinical programs. However, significant net losses and high operating expenses present financial challenges. The positive highlights slightly outweigh the concerns, indicating a cautiously optimistic outlook.Read More>
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                  RARE Stock 12 Month Forecast

                  Average Price Target

                  $91.00
                  ▲(183.14% Upside)
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<div class=\"flexrcb px3 displayflex fonth9_semibold\"><span  style=\"color:#199ca5\">Buy 56,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 3, \t&nbsp;</span>\n              <span  style=\"color:#912767\">Sell 0</span>\n      ","marker":{"lineColor":"#199ca5","enabled":true,"symbol":"circle"}},{"y":41.12,"date":1719792000000,"info":" <span style=\"color:#199ca5\" class=\"mb3 mt2 fonth8_semibold\"> Strong Buy</span>\n            <div class=\"flexrcb px3 displayflex fonth9_semibold\"><span  style=\"color:#199ca5\">Buy 56,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 3, \t&nbsp;</span>\n              <span  style=\"color:#912767\">Sell 0</span>\n      ","marker":{"lineColor":"#199ca5","enabled":true,"symbol":"circle"}},{"y":44.15,"date":1722470400000,"info":" <span style=\"color:#199ca5\" class=\"mb3 mt2 fonth8_semibold\"> Strong Buy</span>\n            <div class=\"flexrcb px3 displayflex fonth9_semibold\"><span  style=\"color:#199ca5\">Buy 43,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 2, \t&nbsp;</span>\n              <span  style=\"color:#912767\">Sell 0</span>\n      ","marker":{"lineColor":"#199ca5","enabled":true,"symbol":"circle"}},{"y":56.78,"date":1725148800000,"info":" <span style=\"color:#199ca5\" class=\"mb3 mt2 fonth8_semibold\"> Strong Buy</span>\n            <div class=\"flexrcb px3 displayflex fonth9_semibold\"><span  style=\"color:#199ca5\">Buy 34,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 2, \t&nbsp;</span>\n              <span  style=\"color:#912767\">Sell 0</span>\n      ","marker":{"lineColor":"#199ca5","enabled":true,"symbol":"circle"}},{"y":56.51,"date":1727740800000,"info":" <span style=\"color:#199ca5\" class=\"mb3 mt2 fonth8_semibold\"> Strong Buy</span>\n            <div class=\"flexrcb px3 displayflex fonth9_semibold\"><span  style=\"color:#199ca5\">Buy 28,\t&nbsp; </span>\n              <span  style=\"color:#828080\">Hold 1, \t&nbsp;</span>\n    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                  Best Analysts Covering RARE

                  1 Year
                  Joon LeeTruist Financial
                  1 Year Success Rate
                  7/17 ratings generated profit
                  41%
                  1 Year Average Return
                  +5.85%
                  reiterated a buy rating 6 days ago
                  Copying Joon Lee's trades and holding each position for 1 Year would result in 41.18% of your transactions generating a profit, with an average return of +5.85% per trade.
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