Exceeding Revenue Expectations
Ultragenyx reported a total revenue of $560 million for 2024, representing a 29% growth over 2023. They exceeded their increased guidance for total revenue, surpassing the upper end of the range.
International Expansion Success
Ultragenyx successfully launched EVKEEZA in Europe, Canada, and Japan, and expanded access in Latin America, Canada, and Turkey. This contributed to a 78% growth in CRYSVITA sales in Latin America and Turkey over 2023.
Clinical Program Advancements
Ultragenyx advanced 6 late-stage programs, including the filing of their first BLA for Sanfilippo syndrome and expected Phase 3 data on UX143 for osteogenesis imperfecta.
Strong Product Performance
CRYSVITA contributed $410 million in revenue, with DOJOLVI contributing $88 million, each showing significant growth over the previous year.