Significant Revenue Growth
Ultragenyx reported $139 million in total revenue for Q3 2024, representing a 42% growth compared to the prior year quarter.
Strong Performance of Crysvita
Crysvita contributed $98 million in revenue, with notable sales in North America, Latin America, Turkey, and Europe.
Breakthrough Therapy Designation for UX143
UX143 for osteogenesis imperfecta received breakthrough therapy designation from the FDA to reduce fracture risk in patients aged 2 and older.
Progress in Gene Therapy Programs
New data from DTX401 for glycogen storage disease type 1a showed a 62% mean reduction in daily cornstarch requirement in crossover patients.
Successful Commercialization Efforts
Generated over $110 million in revenue in Latin America this year, with significant contributions from Crysvita, Mepsevii, Dojolvi, and Evkeeza.