Financial PositionThe company holds a strong balance sheet with $226 million in cash, providing financial runway into 2026.
Regulatory DesignationsNomlabofusp previously received Rare Pediatric Disease Designation, Fast Track Designation, and Orphan Drug Designation from the FDA.
Therapeutic PotentialNomlabofusp has the potential to be the first therapy to address frataxin deficiency, which is the root cause of disease in Friedreich's ataxia.