Clinical DevelopmentNomlabofusp has the potential to be the first therapy to address frataxin deficiency, which is the root cause of disease in Friedreich’s ataxia.
Market PotentialLarimar’s nomla is the most de-risked late-stage program in FA that addresses the root pathophysiology of disease and is establishing a line-of-sight to enter and stake a claim to what may become a multi-billion-dollar FA market.
Regulatory MilestonesNomlabofusp previously received Rare Pediatric Disease Designation, Fast Track Designation, and Orphan Drug Designation from the FDA.