Clinical Trials And Market OpportunityRenewed interest in pociredir’s potential in sickle cell disease (SCD) has emerged following Pfizer’s recent withdrawal of Oxbryta from the market, which has reinvigorated investor discussions about pociredir’s opportunity in this space.
Financial PositionFulcrum ended the quarter with $273.8M in cash, cash equivalents, and marketable securities.
Market Dynamics In Muscular DystrophyFSHD is the second most common form of muscular dystrophy in adults and has no approved therapy, so the opportunity could be substantial.