Clinical EfficacyDeramiocel treatment showed clear and significant slowing of LVEF reduction at 12 months in clinical trials, highlighting its effectiveness in improving cardiac outcomes.
Market Expansion PotentialFunctional outcomes data could be the basis of EU approval, where the DMD market is relatively underdeveloped, indicating potential for market expansion.
Regulatory MilestonesCapricor Therapeutics has completed the BLA submission for DMD cardiomyopathy, indicating progress in regulatory processes.