Global Expansion And Market StrategyExpanding BMRN presence in international markets represents a significant opportunity, as it accounts for about 90% of Voxzogo's total addressable market.
Market Leadership And Competitive EdgeVoxzogo has a high compliance rate of 95%, a ~5-year lead over any potential competitor, a broad US label from birth, a long-term safety database, and growing evidence of benefit beyond growth.
Pipeline And InnovationBMN 333 is highlighted as the company's most important pipeline asset, with management aiming to significantly improve efficacy compared to Voxzogo.