Clinical TrialsThe Independent Data Monitoring Committee found no significant safety concerns in the AMT-191 and AMT-162 studies, allowing QURE to proceed with patient dosing.
Regulatory ProgressQURE reached regulatory alignment with the FDA for accelerated approval of AMT-130, eliminating the need for an additional study and boosting investor confidence.
Therapeutic AdvancementsAMT-130 is poised to become the first disease-modifying treatment for Huntington's disease, with statistically significant results in slowing disease progression.