Clinical ValidationPrecision Bio's in vivo gene editing platform is viewed as a major step towards validation, marked by complete clinical response in first-in-human trial for OTC deficiency.
Market PotentialDTIL is upgraded to Outperform with a potential 100-200% upside, highlighting a favorable risk/reward scenario due to its current valuation being about one-third of its net cash position.
Technological MilestoneARCUS technology now has clinical validation of in vivo delivery and gene insertion, representing an important milestone for the company.