Positive Phase II Study Results for Mavorixafor in Chronic Neutropenia
The Phase II study showed mavorixafor increased mean absolute neutrophil count (ANC) to normal levels as monotherapy and in combination with G-CSF, with 75% of participants reducing their G-CSF dose.
U.S. FDA Approval and Launch of XOLREMDI
X4 Pharmaceuticals received U.S. FDA approval for XOLREMDI (mavorixafor) for WHIM syndrome, and successfully engaged 3,400 targeted immunologists and hematologists.
Strong Financial Position
X4 Pharmaceuticals ended Q3 2024 with cash and equivalents of $136 million, providing a financial runway into late 2025.
Significant G-CSF Reduction Achieved
In the combination group, G-CSF was reduced by 52% on average at month 3 and 70% at month 6.
High Physician Engagement
75% of surveyed healthcare providers reported they would consider prescribing XOLREMDI for WHIM patients.