Significant Revenue Growth
Third quarter 2024 net product sales reached $90.3 million, an 89% increase from the same quarter in 2023. Full-year guidance was raised to $330-$335 million.
Breakthrough Designation for Volixibat
Volixibat received breakthrough therapy designation for cholestatic pruritus in PBC based on the VANTAGE study interim results.
Priority Review for Chenodiol
The FDA granted priority review for the NDA in CTX with a PDUFA date of December 28, 2024.
Positive Operating Cash Flow
Achieved positive operating cash flow for the first time in Q3 2024.
Expansion into Fragile X Syndrome
Introduced MRM-3379, a candidate for Fragile X syndrome treatment, expanding the rare genetic neurology portfolio.