Clinical DataRisks include delays in advancing pipeline candidates into and through clinical assessment and failure to generate favorable clinical data from ongoing programs.
Clinical TrialsThere is a 20% probability of approval for both the Hemophilia A and transthyretin amyloidosis programs, which indicates conservative expectations.
Pipeline RisksRisks include, but are not limited to: delays in advancing pipeline candidates into and through clinical assessment; failure to generate favorable clinical data from ongoing programs, particularly in Hemophilia A and TTR; and possible long-term dilution risk.